"Gene therapy has opened a very interesting chapter. With a single intravenous infusion, we can achieve factor IX levels of around 30-35% after five years in hemophilia B. This is an incredible result," said Flora Peyvandi, professor of Internal Medicine at the University of Milan, during the 29th National Congress of Siset – the Italian Society for the Study of Hemostasis and Thrombosis.
https://www.youtube.com/watch?v=EPboy1sqYBY
